Agios reported the results of the study on Wednesday, and they were mixed. Most patients didn’t experience much of a difference.

When Amy Cohen, 29, finished the New York City Marathon, she broke ground as the first person with the illness to run the 26.2 mile race Amy Cohen became the first-ever person with sickle cell anemia ...

A baby was diagnosed with a brain tumour after he struggled to sit up and use his left hand - symptoms which were initially put down to developmental delays. Jordy Arthur was 10 months old in March, ...

A migrant sex offender who was mistakenly released from prison has claimed he tried to hand himself in to police the day before he was apprehended. Hadush Kebatu told Sky News he approached police on ...